Orphan Drugs: A Critical Overview of Rare Disease Treatments
Introduction Orphan drugs are pharmaceutical agents developed specifically to treat rare diseases, often affecting a small percentage of the population. These drugs play a crucial role in addressing unmet medical needs, as many rare diseases lack effective treatment options. However, their development and distribution face numerous challenges, including high research costs, regulatory hurdles, and limited market potential. What Are Orphan Drugs? Orphan drugs are medications intended…
